Q4 2024 Earnings Call Transcript March 13, 2025 REGENXBIO Inc. beats earnings expectations. Reported EPS is $-1.01, ...

Patients treated with 121 achieved decreased CSF ... 121 is well positioned to be the first gene therapy and onetime treatment for Hunter syndrome that can address neurocognitive decline.

Trump Derangement Syndrome didn’t just rot their brains ... the way the German people justified the way the Nazi government treated Jews – they had it coming for…fill in the blank.

"Oura Ring is not a medical device and is not intended to diagnose, treat, cure, monitor, or prevent medical conditions ...

Rachel Zegler is quite good (and Gal Gadot is not) in Snow White, the latest product from the Disney remake machine. Here's ...

America’s Thrift Store on Canton Road in Marietta is the Olympic stadium of secondhand shopping – massive, slightly overwhelming, and filled with potential record-breaking finds. The no-nonsense ...

In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form of epilepsy, scientists have developed a new gene replacement therapy in ...

Cushing syndrome is caused by long-term exposure to high cortisol levels. Diagnosing the cause can help determine the type of treatment needed. Lifestyle changes can also help with symptoms.

In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...

Thanks to the community, research into a cure for SURF1 Leigh Syndrome is close to reaching a major milestone.

Denali remains on track to submit a BLA for tividenofusp alfa or DNL310 for the treatment of MPS II (Hunter syndrome), under the accelerated approval pathway in early 2025, and is preparing for a ...