Several companies—including JCR Pharmaceuticals, Denali Therapeutics and Regenxbio— have products in the pipeline that could ...

In this new study, the research team wondered if female physical prowess has also been overlooked in a hunter–gatherer ... that one of the most striking features of human anatomy is the ...

A larger-than-normal head is one of the physical characteristics of Hunter syndrome, according to the advocacy group Project Alive. “The prognosis was that he might not make it to his teenage ...

“Mice with Hunter syndrome treated with the HSC gene therapy showed dramatic improvement in their condition, including normalization of working memory problems, and skeletal features such as the ...

Denali’s wholly owned program, DNL310 or tividenofusp alfa, is an Enzyme Transport Vehicle-enabled iduronate-2-sulfatase (IDS) replacement therapy in development for MPS II (Hunter syndrome).

This leads to buildup in the organs and can cause damage over time that affects patients’ physical and mental abilities. RegenXBio gets FDA support for Hunter syndrome gene therapy's accelerated ...

Hunter syndrome is caused by mutations in the iduronate-2-sulfatase (IDS) gene, which leads to a deficiency of the IDS enzyme. Symptoms often begin emerging around age two and include physical ...