That partner, Japan’s Nippon Shinyaku, is handing over $110 million upfront to lead on the commercialization of two gene therapies—RGX-121 for Hunter syndrome and RGX-111 for Hurler syndrome.

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown the ...

Milwaukee should turn its focus to former Texas Rangers hurler David Robertson. He and Kenley Jansen arguably are the best remaining hurlers on the open market right now for the bullpen.

One former member of the Boston Red Sox likely is going to need to find a new home in the near future. The Los Angeles Dodgers officially announced their signing of two-time All-Star Kirby Yates ...

The Chicago Cubs appear poised to challenge for the top spot in the National League Central and reportedly are interested in signing a 33-save hurler before winter's end. Drew VonScio of Newsweek ...

California Institute for Regenerative Medicine (CIRM) has awarded a $5.8 million translational research grant to a scientist at the University of California, Los Angeles (UCLA) to further support the ...

Scientists from Delft, Vienna, and Lausanne discovered that the protein machines that shape our DNA can switch direction ... such as Cornelia de Lange syndrome, linked to SMCs, where the motors ...

While the Baltimore Orioles have made a few key moves this offseason, signing Tyler O'Neill, Andrew Kittredge, Charlie Morton and Tomoyuki Sugano, they still have work to do. They lost Anthony ...

A 2015 report published by a private genomics testing company found that 2% of 345 hot dogs tested contained traces of human DNA. However, it was unclear whether that report was a peer-reviewed ...

Unfortunately, he won't be back in 2025 and reportedly signed a one-year, $10 million deal with the Baltimore Orioles, according to The Athletic's Ken Rosenthal. "Free-agent reliever Andrew ...

A solid place to start might be with a former homegrown hurler. "For all intents and purposes, they (Cardinals) have the exact same roster as four months ago," Bleacher Report's Kerry Miller wrote ...

Daragh and Cian Hayes wrongly believed Ciaran Ryan had become romantically involved with Daragh Hayes’s ex partner Cian Hayes and Daragh Hayes Two brothers of Limerick hurling star Kyle Hayes ...