The FDA has granted fast-track designation to an investigational antisense oligonucleotide to treat individuals with myotonic ...

CHARLESTOWN, Mass. - Solid Biosciences Inc. (NASDAQ:SLDB), a $130.65 million market cap biotechnology company, has been granted Fast Track designation by the U.S. Food and Drug Administration (FDA) ...

Patients with spinal muscular atrophy (SMA) type 2 showed improved motor ability when treated with intrathecal onasemnogene ...

Capricor Therapeutics has completed its submission of a biologics license application (BLA) seeking U.S. approval of deramiocel, the company’s cell therapy for heart muscle disease in people with ...

Arsenal goalscorer Ethan Nwaneri was substituted at half-time against Brighton & Hove Albion because of a muscular injury, Mikel Arteta has said. The 17-year-old opened the scoring for Arsenal in ...

offering new pathways for understanding and treating Duchenne Muscular Dystrophy (DMD). DMD, a severe genetic disorder that causes muscle weakness and shortens lifespans, arises from mutations in ...

offering new pathways for understanding and treating Duchenne Muscular Dystrophy (DMD). A groundbreaking study has shed light on the complex interactions between dystrophin, a protein critical to ...

Nila Morton was born with a rare form of muscular dystrophy called Ullrich, which requires her to rely on a wheelchair Nila Morton Nila Morton, a graduate student at Howard University, was excited ...

Dec. 16, 2024 — A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle degeneration. Researchers have discovered that an ...