Anthony Bergmann; Chief Financial Officer; Capricor Therapeutics Inc. Linda Marban; President, Chief Executive Officer, Director; Capricor Therapeutics Inc. Edward T ...
RGX-202, a DMD gene therapy, has been well tolerated in an ongoing clinical trial and improved motor function for DMD boys, ...
The warning comes amid reports that unregulated therapies are being offered directly to patients, potentially illegally.
The interim data found one child in the Duchenne trial produced more than double the amount of the protein needed to maintain ...