For millions of people, losing muscle isn't just about weakness; it's about losing independence. Whether caused by Duchenne ...

Researchers have discovered a potential therapeutic target in muscular disorders by identifying a previously unrecognized ...

A team has discovered a possible therapeutic approach to repair injured muscles either from aging or degenerative muscle disorders.

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

As it gears up to submit an approval application next year, Wave Life Sciences has presented fresh phase 2 data showing its ...

Regenxbio has reported positive interim data from the Phase I/II portion of its Affinity Duchenne study, which is examining ...

For millions of people, losing muscle isn't just about weakness; it's about losing independence. Whether caused by Duchenne muscular dystrophy, aging or other degenerative conditions, muscle loss can ...

Avidity Biosciences Inc. says will submit an application for accelerated approval to the FDA for del-zota before the end of ...

The company plans to submit a Biologics Licence Application to the US Food and Drug Administration later in 2025 for its DMD ...

For millions of people, losing muscle isn't just about weakness; it's about losing independence. Whether caused by Duchenne muscular dystrophy, aging ...

Giulio Cossu, MD, speaks to the lingering safety concerns related to ex vivo gene therapy in Duchenne muscular dystrophy (DMD) as long-term data are yet to be established.

Precision BioSciences (DTIL) announced the presentation of preclinical data for its PBGENE-DMD development program for the treatment of ...