While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

Pratteln, Switzerland, January 16, 2025 – Santhera Pharmaceuticals (SIX: SANN) announces that the National Institute for Health and Care Excellence (NICE) has issued positive Final Guidance that ...

Dino Ferrari's brief time on the planet proves the old adage that life is short. It is a race, and you never know where the finish line is painted. This 206 GT that bears his name is one of those cars ...

Muscular dystrophy (MD) represents a group of inherited muscle disorders that primarily cause muscle weakness and muscle wasting, though some types of the disease also present with other ...

Duchenne muscular dystrophy (DMD) is a rare genetic pediatric ... First, respondent characteristics (age, gender, annual income, employment status, and education) were explored to determine ...

RNA)’s stock is being fueled by encouraging clinical development of its 3 rare neuromuscular programs — del-desiran for myotonic dystrophy type 1 (DM1), del-zota for Duchenne muscular ...

Joseph Pantginis, an analyst from H.C. Wainwright, reiterated the Buy rating on Astria Therapeutics (ATXS – Research Report). The associated ...

Quince Therapeutics, Inc. , a late-stage biotechnology company dedicated to unlocking the power of a patient's own biology for the treatment of rare diseases, announced the online publication of ...

Hoffmann-La Roche Limited (Roche Canada) is pleased to announce today that Health Canada has authorized Vabysmo® ...

Adapting Electronics To Our Brain Over time, electronic devices have progressively become smaller and more omnipresent in our ...

The National Organization on Fetal Alcohol Syndrome (NOFAS) reports FASD affects around 40,000 infants each year, more than spina bifida, Sudden Infant Death Syndrome (SIDS), cystic fibrosis, cerebral ...

The characteristics of the 33 patients with PM/DM (10 males ... FDG PET findings between patients with PM/DM and non-inflammatory myopathies, such as muscular dystrophy.