Roche and Sarepta Therapeutics have shared positive top-line results from a late-stage study of Elevidys (delandistrogene ...
The gene therapy delandistrogene moxeparvovec-rokl showed clinically meaningful benefits and disease stabilization at 2 years ...
Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...
Qatar Tribune on MSN6d
Qatar: Sidra establishes Gene Therapy Center for rare genetic diseasesThe announcement was made at Arab Health 2025 where Sidra Medicine will highlight its international patient service programmes ...
In year two of the trial, Elevidys demonstrated statistically significant and clinically improvements across three key ...
Entrada Therapeutics (TRDA) announced it had received authorization from the United Kingdom’s Medicines and Healthcare Products Regulatory ...
“You could see I was walking differently. I might have been a bit clumsy at the time. I thought I might have just taken after ...
Research in genetics and biotechnology has advanced by leaps and bounds in recent years, offering new hope for the treatment ...
REGENXBIO is a longtime player in the gene therapy space, but one that’s yet to bring its own therapy to market (in the early ...
KOIN Portland on MSN4d
Vancouver family launches son’s ashes into spaceA Vancouver family is sending their son on one final journey into the stars, where his ashes will eventually transform into a ...
We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder ... between these two conditions, either at the genetic or at the protein level, and might clarify, at least partially ...
The Elevate-44-201 study is a global, two-part, randomized, double-blind placebo-controlled phase 1/2 study evaluating the ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback