While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...
Some types of muscular dystrophy typically affect only males; some people with MD enjoy a normal life span with mild symptoms that progress very slowly; others experience swift and severe muscle ...
Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early ...
Riding recent momentum in the Duchenne muscular dystrophy space, Capricor Therapeutics, Wave Life Sciences, Regenxbio and ...
There are several types of muscular dystrophy. Muscle weakness is a hallmark of each type. But the symptoms can vary and start at different ages. Some muscular dystrophies are mild. Others are ...
The dysferlin protein is primarily responsible for repairing cell membranes. People with certain mutations in the gene coding for dysferlin develop muscular dystrophy—a group of muscle wasting ...
A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...
The dysferlin protein is primarily responsible for repairing cell membranes. People with certain mutations in the gene coding for dysferlin develop muscular dystrophy – a group of muscle wasting ...
The dysferlin protein is primarily responsible for repairing cell membranes. People with certain mutations in the gene coding for dysferlin develop muscular dystrophy – a group of muscle wasting ...
The FDA has granted fast track designation to DYNE-101, a therapy for myotonic dystrophy type 1 (DM1) now in testing in a ...
Ips Heart Inc. has been awarded orphan drug designation by the FDA for its GIVI-MPC stem cell therapy for Becker muscular dystrophy. GIVI-MPC has the unique ability to create new muscle with full ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback