Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, ...

Roche (RHHBY) announced that it will present new data at the Muscular Dystrophy Association, MDA conference, 16-19 March, 2025, in Dallas, ...

Get Instant Summarized Text (Gist) Nanoparticles have been developed to deliver microRNAs to muscle stem cells, offering a potential treatment for Duchenne muscular dystrophy. These nanoparticles ...

today announced that the company will present preclinical data from the PBGENE-DMD program for the treatment of Duchenne muscular dystrophy (DMD) during an oral presentation at the 2025 Muscular ...

If you’re living with Duchenne muscular dystrophy (DMD), planning ahead can help support the success of future education, employment, and housing efforts. Duchenne muscular dystrophy (DMD ...

I have the same rare neuromuscular disease Mats had, known as Duchenne muscular dystrophy. I am also the son of the founders of CureDuchenne, the Newport Beach-based global nonprofit that will use the ...

Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed down) disorder. The condition is ...

Oral Presentation: Title: First-in-human Phase 1 study of orally administered SAT-3247 in healthy volunteers and adult participants with Duchenne Muscular Dystrophy (DMD) Date: Wednesday ...