Data from the EMBARK trial of delandistrogene moxeparvovec in patients with Duchenne muscular dystrophy (DMD) show that ...

Children with SMA given the gene therapy Zolgensma in infancy are maintaining motor milestones after up to 10 years, new ...

The young man died of acute liver injury, a known side effect, Sarepta said in a statement. But the company said the ...

Myotonic dystrophy type 1 (DM1) is the most common adult-onset form of muscular dystrophy and a condition that severely ...

The rapid development of gene therapy options for treating neuromuscular diseases has created new therapeutic options but ...

4. Administered the first dose of a new gene therapy for muscular dystrophy. 5. Implemented an Omnicell inventory management program at WVU Medicine's Mary Babb Randolph Cancer Center, achieving ...

Newborns in Minnesota can now be screened for Duchenne muscular dystrophy (DMD) and guanidinoacetate methyltransferase (GAMT) deficiency. While there is no cure, treatment can make symptoms and ...

Duchenne muscular dystrophy causes progressive muscle degeneration and weakness, but physical exercise should still be part of a comprehensive treatment strategy. Duchenne muscular dystrophy (DMD ...

Therefore, option (c) is the correct answer. — A two-and-a-half-year-old girl has shown no signs of a genetic disorder — known as spinal muscular atrophy (SMA) — becoming the first person in the world ...

Soaking up the Aussie sun, the actor, who grew up in Wales, showcased his muscular torso as he went shirtless while wearing a pair of navy shorts. The star is best known for his breakout role ...

Spinal bulbar muscular atrophy (SBMA) causes a loss of motor neurons in the spinal cord and brainstem. It mainly affects facial and swallowing muscles and the muscles in the arms and legs.

SEOUL – A South Korean student with muscular dystrophy, which has left him mostly paralysed except for his eye movements and speech, has earned a master’s degree by writing his thesis one ...