Contrary to prior data, this study shows that neither eosinophils nor STAT6-mediated IL-4/IL-13 signaling contribute ...

Children's Mercy Kansas City has achieved a significant advancement toward the treatment of rare genetic diseases through the ...

Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early diagnosis, multidisciplinary care, and emerging treatments like gene therapy ...

In addition, the regulator greenlit Calquence’s use as a part of a first-line combo treatment in MCL patients who are ineligible for autologous hematopoietic stem cell transplantation. The news came ...

An Irish woman has launched a fundraiser to help raise money for medical treatment for her seven-year-old son. Una Ennis' son Archie has been diagnosed with Duchenne Muscular Dystrophy - a serious ...

All problems (adverse events) related to a medicine or medical device used for treatment or in a procedure should be reported to the Medicines and Healthcare products Regulatory Agency using the ...

Some types of muscular dystrophy cause irregular heartbeats. Gene therapy. Delandistrogene moxeparvovec (Elevidys) is a gene therapy approved to treat Duchenne MD. It's only prescribed to people ...

What Is Duchenne Muscular Dystrophy? Muscular dystrophies are ... It was the first targeted treatment for this type of mutation and has been shown to help increase the production of dystrophin.

Cell therapy developers, especially early-stage companies, often face significant challenges scaling their manufacturing processes, requiring extensive investment in developing their own methods ...

A first-in-human study of Sana Biotechnology’s transplanted islet cells has shown potential as a possible treatment for type 1 diabetes ... preclinical development of SC451 (HIP-modified stem ...

Ips Heart Inc. has been awarded orphan drug designation by the FDA for its GIVI-MPC stem cell therapy for Becker muscular dystrophy. GIVI-MPC has the unique ability to create new muscle with full ...