The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National ...

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

The US Food and Drug Administration (FDA) has granted Rare Pediatric Disease (RPD) designation to NS-051/NCNP-04, which is ...

According to Dr Ann Agnes Mathew, Consultant Pediatric Neurologist at Bangalore Baptist Hospital, DMD is life-threatening and ...

For Captain Joe Dion, it’s about caring for his family. The 38-year-old father of three took two seasons off from the job ...

Helen G. Cross, 71, of Cleveland died on Sunday, January 19, 2024, in Chattanooga. She was born on May 12, 1953, in Albany, Ky., to the late Clarence Edward and Nellie Gray Cash Cross. She was ...

Most types of muscular dystrophy are hereditary diseases. Researchers have discovered more than 30 genes responsible for causing different types of MD and genetic testing can assess your risk of ...

As a parent and caregiver to three sons with DMD, columnist Betty Vertin's definition of what success looks like has changed over the years.

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

Japan’s Nippon Shinyaku is continuing to scoop up the international rights to some intriguing drugs, this time penning a $686 ...

Spinraza remains a big product for Biogen, but has seen its sales go into reverse as competition in SMA treatment has emerged ...

An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines Agency (EMA) considerate it as an alternative than the current lower ...