The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National ...

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

Altruism values for treatments of rare, severe pediatric diseases have not been estimated. This study found the altruism value for a hypothetical new Duchenne muscular dystrophy treatment to be $80 ...

The various types of MD affect more than 50,000 Americans. Through advances in medical care, children with muscular dystrophy are living longer than ever before. Muscular dystrophy is caused by ...

“I never expected for this to happen to my little boy and it makes me petrified for the future. Me and my family have decided to take part in the Manchester half marathon in October which will ...

Only males can get certain types of muscular dystrophy because of how the disease is inherited. Children who are born with muscular dystrophy usually develop normally for the first few years of life.

Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne muscular dystrophy (Duchenne), will host its sixth in-person Duchenne Healthcare Professionals ...

WASHINGTON, Jan. 15, 2025 /PRNewswire/ -- Parent Project Muscular Dystrophy (PPMD), a nonprofit ... innovations in care including newborns, infants, and toddlers, and updates in clinical research ...

Santhera Pharmaceuticals’ Agamree (vamorolone) has been accepted by the Scottish Medicines Consortium (SMC) to treat Duchenne ...

This follows confirmation that no appeals were received against the Final Draft Guidance (FDG) recommendation announced on December 10, 2024. Following this, Santhera has already started launch ...

A trial team led by Latham’s Mike Morin and David Frazier and Finnegan’s William (Bill) Raich helped Sarepta Therapeutics ...

For Captain Joe Dion, it’s about caring for his family. The 38-year-old father of three took two seasons off from the job ...