While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...
(RTTNews) - Sarepta Therapeutics, Inc. (SRPT) Monday reported positive topline results from Part 2 of the Phase 3 study, dubbed EMBARK, of its gene therapy Elevidys approved for the treatment of ...
The gene therapy delandistrogene moxeparvovec-rokl showed clinically meaningful benefits and disease stabilization at 2 years ...
European regulators are to review Sarepta Therapeutics’ Duchenne muscular dystrophy drug, eteplirsen – a drug that has sparked controversy in the US, where it was approved by the FDA against ...
Learn More Genetic Causes of Muscular Dystrophy Is muscular dystrophy fatal? Some types of muscular dystrophy can be fatal. Certain types, including Duchenne muscular dystrophy, can lead to problems ...
Body dissatisfaction can be minor, too bad my nose is so big, or it can be severe, I hate everything about my body.Once you start to think that you have a flaw, your mind runs with the distraction ...
Muscle strength grading is used to categorize muscle strength on a scale of 0 to 5 in relation to the expected strength for a muscle. One of the more common methods is a hands-on test called the ...