Sickle cell anemia patient reunites with Long Island doctors whose gene therapy treatments made him symptom-free
Sebastien Beauzile, 21, became the first person in New York state to be made symptom-free of sickle cell disease after ...
Warwick boy authors "Ultimate Lymphedema Warrior" to raise awareness about rare condition
A 10-year-old Warwick boy is raising awareness about a rare condition in children. "One of the character's name's is Penelope ...
Threat to son's treatment for rare disease 'agony'
A mother has spoken about her "painful" experience over the potential end to her son's life-enhancing treatment for a rare ...
inews.co.uk3d
30 low-effort health tips the experts swear by
The most elaborate wellness routine won't work if you neglect the basics. Dieticians, personal trainers, GPs, physios and ...
AskBio Advances Gene Therapy Clinical Trial for Limb-Girdle Muscular Dystrophy Type 2I/R9 with Dosing of First Participant in Second Cohort
AskBio Inc. (AskBio), a gene therapy company wholly owned and independently operated as a subsidiary of Bayer AG, today announced the advancement of the Phase 1/Phase 2 LION-CS101 clinical trial of ...
The Republic14d
A child dies of Ebola in Uganda, raising concern over disease surveillance in outbreak
KAMPALA, Uganda (AP) — A 4-year-old child became the second person to die ... Tanzania declared an outbreak of the Ebola-like Marburg disease in January, and in December, Rwanda announced ...
BBC15d
US measles outbreak kills child for first time in a decade
according to the Centers for Disease Control (CDC). Currently, there are nine cases reported in New Mexico, four of whom are children. Kennedy, a vaccine sceptic in the past, said that measles ...
STAT15d
To fight for those with rare diseases, Trump must reform and modernize the FDA thoughtfully
often fatal genetic disorder known as Pompe disease. Thanks to a lifesaving therapy pioneered by my own biotech start-up, Megan was by our side during that speech. She remains healthy and vibrant ...
El País in English15d
Science finds explanation for disease that leaves children ‘frozen’
and partly explains the symptoms of the disease. “Tango2 traps fats and prepares them for combustion. The cells of children with TDD have a reduced capacity to do this, so they are literally deprived ...
Associated Press16d
Harsh flu season has health officials worried about brain complications in children
The Centers for Disease Control and Prevention estimates 19,000 people have died from the flu so far this winter, including 86 children. Thursday, the CDC reported at least nine of those children ...
WION16d
Texas measles death: Unvaccinated child dies amid growing outbreak. This is what anti-vaxxer health secy RFK Jr said
In Texas, United States, an unvaccinated child died from measles, revealed authorities on Wednesday (Feb 26), marking the first US fatality from the highly contagious disease since 2015 when a woman ...