What is Guillain-Barré syndrome? Guillain-Barré syndrome (GBS) is also called acute inflammatory demyelinating polyradiculoneuropathy (AIDP). It's a neurological disorder in which the body's immune ...

Sadie Haywood was diagnosed with Sanfilippo Syndrome at just three months old which left her with inability to walk or talk ...

Denali Therapeutics' ALS drug DNL343 failed to show efficacy, leading to the discontinuation of the trial extension. Analysts now focus on its Hunter syndrome drug.

Eliza O'Neill suffers from Sanfilippo Syndrome and a walk/run is being held to raise money to fund research for the disease.

The Novato-based maker of biopharmaceutical treatments for rare diseases plans to release this year a new gene therapy for Sanfilippo syndrome, a rare metabolism disorder. Ultragenyx ...

The company expects to launch a new gene therapy for Sanfilippo Syndrome, a rare metabolism disorder, in 2025. The company also reported a reduced net loss in 2024 of $569.83 million.

Chronic fatigue syndrome — also known as myalgic encephalomyelitis/chronic fatigue syndrome (ME/CFS) OR systemic exertional intolerance disease (SEID)— is a serious, chronic illness that can ...

We sell different types of products and services to both investment professionals and individual investors. These products and services are usually sold through license agreements or subscriptions ...

She and a group of local women believed Rowan had MPS 3A, more commonly known as Sanfilippo syndrome. A few weeks later, a geneticist confirmed the devastating news: Rowan had Sanfilippo.