An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

More than 150,000 people are affected by muscular dystrophy in the UK - 30,000 suffer directly as a result of their condition but a further 120,000 people including families and carers have had ...

A patient has died while taking a closely watched gene therapy for muscular dystrophy. Sarepta Therapeutics announced the ...

A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

Duchenne muscular dystrophy causes progressive muscle degeneration and weakness, but physical exercise should still be part of a comprehensive treatment strategy. Duchenne muscular dystrophy (DMD ...

Colton Belluzzo was diagnosed with a form of muscular dystrophy when he was a baby. The disease has weakened his muscles over time. But he and his family now have good reason to be optimistic.