RGX-202, a DMD gene therapy, has been well tolerated in an ongoing clinical trial and improved motor function for DMD boys, ...

ROCKVILLE, MD, USA I March 19, 2025 I REGENXBIO Inc. (Nasdaq: RGNX) today reported new, positive interim data from two additional patients in the Phase ...

Posters presented at the 2025 Muscular Dystrophy Association Clinical & Scientific Conference highlight the complex care ...

Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, ...

Myotonic dystrophy type 1 (DM1) is the most common adult-onset form of muscular dystrophy and a condition that severely ...

Sarepta Therapeutics (SRPT) stock drops 25% as the company reports a patient death linked to Elevidys, its gene therapy developed with Roche (RHHBY). Read more here.

For the fourth consecutive year, Han-Dee Hugo’s, 1190 Long Ferry Road, Salisbury will be hosting a MDA Festival to raise ...

Title: RGX-202, an investigational gene therapy for the treatment of Duchenne Muscular Dystrophy: Interim clinical data (O75 ... Enhanced therapeutic potential of a microdystrophin with an extended ...

A family out of New Braunfels is in need of an accessible van to help support three brothers with Duchenne Muscular Dystrophy (DMD ... Trope The abandoned TWA terminal, relic of the golden ...

"I just feel like a different person than when before I joined the team." COOPER HAS MUSCULAR DYSTROPHY CAN ONLY GET AROUND WITH HIS WHEELCHAIR.. AND NOW FINDING HIS PLACE IN THE SOUTH BURLINGTON ...

Few, though, have ever heard of the movement from which they took their principal inspiration: muscular Christianity. The term sounds odd indeed, conjuring up images of Jesus with an impressively ...

Max, Rowen, and Charlie all live with Duchenne muscular dystrophy (DMD). Rowen’s fifth birthday cake was adorned with his Power Rangers figures. When Charlie transitioned from a crib to a big-boy bed, ...