From February 12, all newborn babies will be offered screening for spinal muscular atrophy (SMA), a rare progressive neuromuscular disease. SMA will be one of more than 20 other rare disorders ...

A Boston-area biopharmaceutical firm has submitted a biologics license application to the FDA for its investigational, fully ...

Biogen (NASDAQ:BIIB) shares experienced a change in market expectations as Cantor Fitzgerald revised the company's price target. The new target has been set at $206.00, a decrease from the previous ...

From February 12, all newborn babies will be offered screening for spinal muscular atrophy (SMA), a rare progressive neuromuscular disease. SMA will be one of more than 20 other rare disorders ...

Ionis Pharmaceuticals, Inc. (NASDAQ:IONS) stock has touched a 52-week low, dipping to $31.24, as investors respond to a ...

Novartis' programme providing free access to its spinal muscular atrophy (SMA ... to market its antisense-based therapy Spinraza (nusinersen) since 2016, while Roche got a green light for its ...

In surveys, parents of children with SMA and healthcare professionals in Sweden note the many ways the pandemic affected ...

Novartis is on the final straight to approval of its spinal muscular atrophy (SMA ... presence on the market of Biogen’s Spinraza (nusinersen), an antisense drug given by injection into the ...

Three people with a muscle-destroying disease destined to worsen got a little stronger when an implanted device zapped their ...

In a small human trial in SMA patients neurostimulation sessions improved motoneuron function, reduced fatigue, and improved leg muscle strength and walking.

A new drug-free, minimally invasive intervention targets the root cause of progressive loss of neural function in spinal muscle atrophy (SMA), an inherited neuromuscular disease.

Scholar Rock is asking the U.S. Food and Drug Administration to approve apitegromab for people with spinal muscular atrophy.