Longtime drug developer Suma Krishnan was 51 when she cofounded Krystal Biotech. Now the company has one gene therapy on the ...

Biogen raised its annual profit forecast on Thursday, betting on strong demand for its rare disease drugs such as Skyclarys ...

(Reuters) -Biogen raised its annual profit forecast on Thursday, betting on strong demand for its rare disease drugs such as ...

CRISPR gene editing shows potential for treating genetic diseases. Explore how it may impact Down syndrome treatment and future healthcare ethics.

Gleason enjoyed a low profile as DOGE was thrust into the spotlight and as Musk and Trump eventually had their falling out.

A Fontana child is fighting for her life against a rare genetic disorder called Batten disease while her parents are trying ...

Strategic IP expansion protects federated learning technology driving pharma partnerships, biosecurity initiatives, and ...

A Bridgewater mosquito tested positive for EEE, a very rare but potentially fatal disease in humans spread through mosquito bites. What to know.

A study spearheaded by researchers at Stanford Medicine reports a substantial increase in cases of acute necrotizing ...

The survey primarily focused on rare disease patients between the ages of 16 and 23, as well as caregivers between 25 to 55 years old. Hemophilia, albinism, cystic fibrosis and Gaucher disease were ...

Oregon will initially focus on providing lower-cost therapies for people living with sickle cell disease, a genetic blood ...

Yonker is a co-inventor on a patent for zonulin antagonists to treat MIS-C, as are two other co-authors. Co-authors also ...