Hence, regular pulmonary exams are done, physiotherapists are called in to teach breathing exercises, and if necessary, ventilators are prescribed for sleep or 24/7 use. One day or night struggling to ...

Early results obtained for the SMA patients demonstrated that, in those with elevated levels of neurofilament light chain (NfL), a marker of nerve cell damage, initiation of salanersen led to mean ...

Eden isn’t my only little playmate. Some of my young friends like to go for rides on the back of my wheelchair or on my lap. They might pretend I’m a taxi or a train or a ferry … or a very convenient ...

Long-term data on Spinraza treatment ‘scarce’ In clinical trials, Spinraza showed clinically meaningful benefits, including the achievement of motor milestones, improved motor function, and a lower ...

On the afternoon of July 7, 1997, a sickening thud and screams hailed from the front yard. Our older children, Matthew, 10, and Katie, 7, had been playing with our two dogs when one of them, Duffy, ...